Therapeutic category guide

Rare Disease medication references.

Browse 48 Rare Disease medication profiles and 116 dated European package references for transparent, case-specific comparison. Figures are informational catalog references, not live quotes or guarantees of availability.

Browse Rare Disease references ↓Review the methodology

Medication profiles48

Package references116

European references€2,376.09 – €85,911.43

Review typePackage-specific

Crawlable category index

Rare Disease medications A-Z

Open a medication profile to review its exact listed formats, estimated medicine cost references and source limitations. Different strengths and packages should not be treated as interchangeable.

AGAMREEVamorolone2 package refsfrom €4,540.09 ALYFTREKVanzacaftor, Tezacaftor, Deutivacaftor4 package refsfrom €15,529.44 AmmonapsSodium Phenylbutyrate2 package refsfrom €2,497.35 BrineuraCerliponase alfa1 package reffrom €23,719.79 BylvayOdevixibat4 package refsfrom €3,822.88 CarbagluCarglumic acid3 package refsfrom €3,175.01 Carglumic acidCarglumic acid3 package refsfrom €2,393.82 Carglumic acid Zentivacarglumic acid1 package reffrom €5,568.16 CerdelgaEliglustat2 package refsfrom €26,363.49 Cerezymeimiglucerase1 package reffrom €17,732.06 CufenceTrientine2 package refsfrom €5,238.51 CystadropsMercaptamine2 package refsfrom €2,921.45 ElapraseIdursulfase2 package refsfrom €5,652.91 EvenityRomosozumab1 package reffrom €2,963.29 Fabrazymeagalsidase beta2 package refsfrom €7,921.47 GalafoldMigalastat1 package reffrom €20,977.69 IsturisaOsilodrostat3 package refsfrom €2,806.89 KuvanSapropterin4 package refsfrom €3,705.05 LoargysPegzilarginase1 package reffrom €8,093.41 MiglustatMiglustat5 package refsfrom €7,063.94 Miglustat Accordmiglustat1 package reffrom €8,477.31 Miglustat Bluefishmiglustat1 package reffrom €8,433.00 Miglustat Gen.Orphmiglustat2 package refsfrom €7,063.94 MyaleptaMetreleptin5 package refsfrom €2,376.09 NaglazymeGalsulfase1 package reffrom €3,450.19 Nitisinone DipharmaNitisinone3 package refsfrom €3,421.49 NormosangHemin1 package reffrom €5,559.19 OpfoldaMiglustat1 package reffrom €2,614.70 ORFADINNitisinone8 package refsfrom €2,838.99 Osenveltdenosumab1 package reffrom €2,605.20 PalynziqPegvaliase1 package reffrom €4,616.30 PombilitiCipaglucosidase alfa3 package refsfrom €2,930.48 ReplagalAgalsidase alfa2 package refsfrom €4,178.93 SapropterinSapropterin10 package refsfrom €3,229.28 Sapropterin ALsapropterin1 package reffrom €3,354.29 Sapropterin betasapropterin1 package reffrom €3,354.29 Sapropterin Dipharmasapropterin5 package refsfrom €3,229.28 Sapropterin Purensapropterin1 package reffrom €3,633.96 Sapropterin-ratiopharmsapropterin1 package reffrom €3,587.82 TeriparatidFully synthetic teriparatide3 package refsfrom €2,398.10 TerrosaTeriparatide1 package reffrom €2,476.32 TrientinTrientine3 package refsfrom €5,123.48 Trientine Waymadetrientine1 package reffrom €5,237.36 UcedaneCarglumic acid1 package reffrom €6,058.17 VprivVelaglucerase alfa3 package refsfrom €3,927.00 YargesaMiglustat1 package reffrom €7,536.81 ZavescaMiglustat6 package refsfrom €7,063.73 ZokinvyLonafarnib2 package refsfrom €24,106.81

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